Rare Disease Advocacy World focus on the growing trend of advocacy groups influencing regulation, is having a fantastic sessions
INFLUENCING DRUG DEVELOPMENT –The role of the patient is changing once more. Rare Disease Advocacy World will kick off with industry-led investigation into the impact of patient-industry collaboration.
ADVOCACY IN ACTION- Parent Project Muscular Dystrophy (PPMS), PTC Therapeutics and EveryLife Foundation for Rare Diseases will provide practical insight into how patient groups can impact policymaking and orphan drug development, through realworld examples.
ACCESS-‘Right to Try’ : Rare Disease Advocacy World is facilitating a multi-stakeholder examination of the latest access strategies, and how they will impact the review of new therapies for rare diseases.
NATIONAL PATIENT ORGANIZATIONS- US, South Africa, Australia, Colombia, New Zealand, Japan, India and Europe will also be discussing the opportunities for rare disease research and development in their respective regions.
During this three days, you could enjoy discussions on topics like:
- FUTURE OF ORPHAN DRUGS
- PRICING & REIMBURSEMENT
- APPROVAL & ACCESS
- M&A AND COMMERCIALIZATION
- PATIENT-CENTRIC RESEARCH
- REAL-WORLD EVIDENCE
- MARKETING & COMPETITIVENESS
- GENE THERAPY
- SCIENTIFIC INNOVATION
- REGIONAL MARKET ANALYSIS
- BIOSIMILARS
- ROUNDTABLES
